Links

Careology Clinical Homecare

European Organisation for Rare Diseases

European Platform for Patients’ Organisations, Science and Industry

Fabry Support and Information Group

Genetic and Rare Disorders Association

Genzyme Clinical Trials

Genzyme Pharmaceuticals

Irish Platform for Patients’ Organisations, Science and Industry

Irish Society for Mucopolysaccharide Diseases

Medical Research Charities Group

National Centre for Inherited Metabolic Disorders

National Institute of Health Office for Rare Diseases Research

Orphanet

Rapsody Online

Shire Pharmaceuticals

UK Society for Mucopolysaccharide Diseases






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